Gene therapy provides a viable path to curing sickle cell disease by using a viral vector to deliver a functional beta-globin gene into patient stem cells.

“So when we talk about gene therapy for us we basically take the HIV virus and we disarm it so now it's an empty school bus and we put the gene that we want to get into the patient the defected Gene in our case the betaglobin Gene and we make a bunch of school buses with a bunch of betaglobin genes i”