Gene therapy represents a fundamental and effective way to cure diseases by correcting DNA at the molecular level.

“right at the DNA level correcting the DNA is the most fundamental way that we can cure disease as as human beings as as we see it”

Gene therapy uses viruses as tools to deliver functional genes or correct mutations to treat diseases.

“this is using viruses as medicines so historically we have used these to treat single Gene genetic disorders but we can use these much more broadly now”

Gene replacement therapy using deactivated viruses to deliver healthy genes is a highly effective, scientifically validated method for curing genetic conditions like thalassemia.

“The age virus, we deactivate it. We load it up with the beta globin gene which is the adult hemoglobin gene which is the defect for cickle cell disease and thealosmia. We make enough of these genes we give the patient chemotherapy to clean his bone marrow so that we can infuse the gene therapy.”